Author's posts
One Reporter, Four Families, Six Scientists and the Search to Cure a Rare Disease
A WSJ reporter followed a group of families and scientists trying to accelerate the development of a drug to treat Niemann-Pick Type C disease, a rare and fatal cholesterol metabolism disorder known as NPC that strikes primarily children.
Robots to Cure Rare Diseases: A Reddit Ask Me Anything (AMA)
For years, Christopher P. Austin has been trying to develop a way for science to build a better partnership with patients. Dr. Austin and the Journal’s Amy Dockser Marcus are answering questions now.
