As BioMarin turns to commercialization of Roctavian, we will likely hear more about how warranties could help gene therapies overcome payer reimbursement hurdles.
Activists Howard and Norma Lotsof devote their lives to the study of ibogaine to help people with addiction and mental illness. Director Lucy Walker humanizes suffering.
Viroids and virusoids are the smallest known pathogens. They have traditionally been considered fairly uncommon; new research challenges this assumption.
This article will discuss some of the most promising gene therapies for age-related macular degeneration, including ADVM-022, RGX-314, GT-005, and HMR59.
Contrary to previous assumptions, hepatitis D virus-like agents seem to be active in a range of different animal species, from fish all the way to termites.